Gene Therapy: A Conversation With Drs Benke & Ultragenyx
Many of us have questions about future CDKL5 treatment options, especially concerning gene therapy. Come learn about genetic therapy approaches in CDKL5 Deficiency Disorder.
We invite you to join us for a webinar on November 16 at 4 PM PT/7 PM ET with Drs Tim Benke, from the University of Colorado, and Ultragenyx. Together they will expand on the presentation “Preclinical Evaluation of AAV9-CDKL5 Gene Therapy” given this past June during the CDKL5 Family Conference which was hosted by the CDKL5 Alliance.Read More
Marinus Expanded Access Program for Ganaxolone
We asked Marinus to tell us more about their new Expanded Access Program (EAP) for ganaxolone.Read More