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Roadmap to a Cure

Estimated Timelines and Costs

Mouse Models – COMPLETED

IPS CELLS  COMPLETED

ZEBRAFISH LINE – COMPLETED

PROTEIN TARGET IDENTIFICATION – IN PROGRESS

DRUG DISCOVERY, SCREENING AND DEVELOPMENT – IN PROGRESS

PHASE I (DRUG) CLINICAL TRIAL

PHASE II (PILOT) CLINICAL TRIAL – SOTICLESTAT TRIAL COMPLETE

PHASE III CLINICAL TRIAL – MARIGOLD TRIAL COMPLETE

CDKL5 CLINICAL CONSORTIUM – IN PROGRESS

DATABASE – IN PROGRESS